RARE DISEASE INNOVATION AND PARTNERING SUMMIT

Patient and Caregiver Perspectives –
Explore New Developments in Cures, Community, Collaboration and the Care Continuum for Patients and Caregivers

Science Luminaries –
Advancements in Gene Therapy that Are Tearing Down Barriers to Discovery in Rare Disease

Regulatory and Policy Update Address –
Legislative Updates and New Initiatives within the FDA’s Orphan Drug Program

Focus on Funding –
The Impact of Disruptive Investors, Drivers of Value and Funding Models for Success

Technology Spotlight –
Artificial Intelligence (AI) and Advanced Data Analytics — Reshaping Complex Diagnostics and Decision-Making in Rare Disease Drug Development